Director, Scientific Affairs

Job description

MISSION: Mirum Pharmaceuticals is a biopharmaceutical company dedicated to transforming the treatment of rare diseases. We are passionate about advancing scientific discoveries to become important medicines for rare disease patients. We are collaborative, creative, and experienced professionals and we’re looking to augment our team with other individuals who embody our values: care, be real, get it done, and have fun, seriously. POSITION SUMMARY: The position will lead Scientific Affairs activities that support the overall strategic plan directed towards the diagnosis and management in rare disease. This individual will serve as a genetics and disease state expert and support all appropriate activities across the company. JOB FUNCTIONS/RESPONSIBILITIES: Key activities include: - Leading data generation plans to address evidence gaps in the therapeutic area. - Driving real-world evidence activities (e.g., phase IV studies, managed access programs, etc.) to inform regulatory, commercial and access requirements. - Supporting the analyses and dissemination of data from real-world registries and data repositories for the therapeutic area. - Overseeing secondary analyses of clinical tria...